Premarket Approval (PMA)

Premarket Approval (PMA) is the most stringent type of device marketing application required by the FDA. PMA is required for Class III devices -- those that support or sustain human life, are of substantial importance in preventing impairment of human health, or present a potential unreasonable risk of illness or injury. The PMA process requires the applicant to demonstrate reasonable assurance of safety and effectiveness, typically through valid scientific evidence including clinical studies.

When PMA is Required

Under Section 515 of the FD&C Act and 21 CFR 814, PMA is required for:

  • Class III devices that were on the market before the 1976 Medical Device Amendments and for which FDA has called for PMAs (preamendment devices)
  • Post-amendment Class III devices for which no predicate device exists and De Novo is not appropriate (due to high risk)
  • Devices found Not Substantially Equivalent (NSE) through the 510(k) process that are classified into Class III

PMA Application Contents

A PMA application must contain sufficient valid scientific evidence to demonstrate reasonable assurance of safety and effectiveness. Per 21 CFR 814.20, required sections include:

SectionContents
Device DescriptionComplete device description including pictorial representations, engineering drawings, composition, principles of operation, and each component or ingredient
Indications for UsePrecise statement of the conditions or diseases to be diagnosed, treated, prevented, cured, or mitigated, including the target patient population
Manufacturing InformationManufacturing methods, facilities, quality control procedures; compliance with 21 CFR 820 (QSR) is expected
Nonclinical Laboratory StudiesBench testing, animal studies, biocompatibility (ISO 10993), electrical safety, software verification and validation, shelf life/reliability testing
Clinical InvestigationsClinical study reports including study protocols, patient demographics, safety and effectiveness endpoints, statistical analysis, adverse events; must comply with 21 CFR Parts 50, 56, and 812
LabelingProposed labeling including physician labeling, patient labeling, and IFU per 21 CFR 801
BibliographyPublished reports of investigations, safety, effectiveness, and any adverse events relevant to the device

Clinical Data Requirements

Clinical investigations for PMA typically require an approved Investigational Device Exemption (IDE) under 21 CFR 812 for significant risk devices. Key requirements include:

  • IDE approval: Required before beginning a clinical study of a significant risk device in the U.S.
  • IRB oversight: All clinical investigations must be approved and overseen by an Institutional Review Board (21 CFR 56)
  • Informed consent: Subjects must provide informed consent per 21 CFR 50
  • Good Clinical Practice: Studies should follow GCP guidelines and 21 CFR 812 requirements
  • Statistical rigor: Pre-specified endpoints, adequate sample size, appropriate statistical analysis plan
  • Multi-center studies: Often preferred by FDA to demonstrate generalizability of results

Advisory Panel Review

FDA may refer a PMA to an advisory panel of outside experts for review and recommendation. The panel meeting is a public proceeding where the panel reviews the PMA, hears presentations from the applicant and FDA, and provides a recommendation on approvability. The panel's recommendation is advisory; the FDA makes the final decision.

FDA typically convenes an advisory panel for novel technologies, first-of-kind devices, or when the risk-benefit assessment is complex. Panels consist of physicians, scientists, and patient/consumer representatives with relevant expertise.

PMA Supplements

After PMA approval, changes to the device, labeling, or manufacturing require PMA supplements (21 CFR 814.39). Types of supplements include:

Supplement TypeWhen RequiredReview Timeline
Original PMA SupplementChanges that affect safety or effectiveness (e.g., new indications, design changes requiring clinical data)180 days
Panel-Track SupplementSignificant changes that may require advisory panel review180 days
180-Day SupplementChanges in labeling, manufacturing process, or device modifications not requiring clinical data180 days
Real-Time SupplementMinor manufacturing changesReviewed during facility inspection
30-Day NoticeManufacturing changes enhancing device safety30 days (may implement if no objection)

PMA vs. 510(k) Comparison

Attribute510(k)PMA
Legal StandardSubstantial equivalenceReasonable assurance of safety and effectiveness
Typical Device ClassClass I (with 510(k)) and Class IIClass III
Clinical DataSometimes requiredAlmost always required (pivotal clinical trial)
Review Time (target)90 days180 days (plus panel review time if applicable)
User Fees (FY2024)$22,550 (standard); $5,637 (small business)$442,026 (standard); $110,507 (small business)
Post-MarketMDR, corrections/removalsMDR, corrections/removals, annual reports, post-approval studies